HCP Resources
One of the core aspects of our approach to corporate social responsibility is to foster patient access to innovative rare and life-threatening disease treatments. Access to therapy is achieved by scientists and providers working in concert to facilitate effective disease treatment protocol.
Our medical team is committed to providing accurate, up-to date and balanced scientific information that enables health care providers to make informed decisions.
If you have a medical product information inquiry, please contact our team via email.
Physicians based in:
Asia-Pacific: apacmedinfo@ptcbio.com
Brazil: brasilmedinfo@ptcbio.com
Canada: camedinfo@ptcbio.com
EMEA (Europe, Middle East and Africa): medinfo@ptcbio.com
Japan: japanmedinfo@ptcbio.com
Latin America: latammedinfo@ptcbio.com
Russia: rumedinfo@ptcbio.com
United States: USMedInfo@ptcbio.com
Countries Not Listed: medinfo@ptcbio.com
For adverse event reporting, please contact pharmacovigilance@ptcbio.com. For all other inquiries, email info@ptcbio.com.
A hub for the latest medical information on rare disease
MEDhub provides HCPs worldwide with:
- Early and accurate diagnosis and management of rare disease
- Best practice information
- Abstracts, posters, webinars, and presentations from medical congresses
- The latest scientific data and expert insights on rare disease across neuromuscular, CNS, and more
Phenylketonuria (PKU) Resources for HCPs
Join the conversation about Phenylketonuria (PKU)
AADC Deficiency Resources for HCPs
Browse our library of websites below to learn more about aromatic L-amino acid decarboxylase (AADC) deficiency, and access resources to share with your patients in clinical practice.
- Australia (English)
- Brazil (Português)
- Pan-Europe (English)
- Germany (Deutsch)
- Italy (Italian)
- Nordics/Baltics/BeNeLux (English)
- US (English)
Información médica
Nuestro equipo médico está comprometido a proporcionar información científica precisa, actualizada y equilibrada que permita a los profesionales de la salud tomar decisiones informadas.
Si tiene una consulta de información médica, comuníquese con nuestro equipo por correo electrónico: medinfo@ptcbio.com
Para comunicación de sospecha de reacciones adversas, por favor contacte con pharmacovigilance@ptcbio.com
Recursos para profesionales de la salud

Visite PTC Campus, la plataforma de PTC dirigida a profesionales sanitarios, para acceder a seminarios web, videos y otros recursos de interés.
PTC Campus está dirigido exclusivamente al profesional sanitario facultado para prescribir o dispensar medicamentos y requiere un registro previo.